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Co-authors
- Seng H. ChengAlexion, AstraZeneca Rare DiseaseVerified email at alexion.com
- Pablo SardiVerified email at genzyme.com
- C. Frank BennettIonis PharmaceuticalsVerified email at ionisph.com
- Kerry J. ResslerMcLean Hospital, Harvard Medical SchoolVerified email at mclean.harvard.edu
- Don W ClevelandUniversity of California at San DiegoVerified email at UCSD.EDU
- Catherine O'RiordanVerified email at sanofi.com
- Jasmeer ChhatwalAssociate Professor of Neurology, Massachusetts General Hospital, Brigham and Women's HospitalVerified email at partners.org
- Krystof BankiewiczProfessor, Endowed Chair, University of California San FranciscoVerified email at ucsf.edu
- Scott A. HeldtUniversity of Tennessee Health Science CenterVerified email at uthsc.edu
- john bringasuniversity of california san franciscoVerified email at ucsf.edu
- Lluis SamaranchAssistant Professor, Neurological Surgery, The Ohio State UniversityVerified email at osumc.edu
- John ForsayethVerified email at ucsf.edu
- Michael HaydenKillam Professor, University of British ColumbiaVerified email at cmmt.ubc.ca
- Abraham ScariaAGTCVerified email at agtc.com
- Frank RigoSenior Vice President, Ionis PharmaceuticalsVerified email at ionisph.com
- Mahmoud A. PouladiAssociate Professor, Department of Medical Genetics, University of British ColumbiaVerified email at ubc.ca
- Christopher T. FrenchNorthern Arizona Univ.Verified email at nau.edu
- Michael SchlossmacherSenior Scientist, Ottawa Hospital Research InstituteVerified email at ohri.ca
- Thomas TamsettNovartisVerified email at novartis.com
- Jerusha NaidooUniversity of California San FranciscoVerified email at ucsf.edu