Steve Wilton
Steve Wilton
Foundation Chair in Molecular Therapies, Murdoch University
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Zitiert von
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Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2 …
S Cirak, V Arechavala-Gomeza, M Guglieri, L Feng, S Torelli, K Anthony, ...
The Lancet 378 (9791), 595-605, 2011
Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-escalation, proof-of …
M Kinali, V Arechavala-Gomeza, L Feng, S Cirak, D Hunt, C Adkin, ...
The Lancet Neurology 8 (10), 918-928, 2009
Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
J Alter, F Lou, A Rabinowitz, HF Yin, J Rosenfeld, SD Wilton, TA Partridge, ...
Nature medicine 12 (2), 175-177, 2006
Regulation of eukaryotic gene expression by the untranslated gene regions and other non-coding elements
LW Barrett, S Fletcher, SD Wilton
Cellular and molecular life sciences 69, 3613-3634, 2012
ALS genetics, mechanisms, and therapeutics: where are we now?
R Mejzini, LL Flynn, IL Pitout, S Fletcher, SD Wilton, PA Akkari
Frontiers in neuroscience 13, 1310, 2019
Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse
QL Lu, CJ Mann, F Lou, G Bou-Gharios, GE Morris, S Xue, S Fletcher, ...
Nature medicine 9 (8), 1009-1014, 2003
Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse
CJ Mann, K Honeyman, AJ Cheng, T Ly, F Lloyd, S Fletcher, JE Morgan, ...
Proceedings of the National Academy of Sciences 98 (1), 42-47, 2001
A mutation in the α tropomyosin gene TPM3 associated with autosomal dominant nemaline myopathy
NG Laing, SD Wilton, PA Akkari, S Dorosz, K Boundy, C Kneebone, ...
Nature genetics 9 (1), 75-79, 1995
Antisense oligonucleotide-induced exon skipping across the human dystrophin gene transcript
SD Wilton, AM Fall, PL Harding, G McClorey, C Coleman, S Fletcher
Molecular Therapy 15 (7), 1288-1296, 2007
Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides
SD Wilton, F Lloyd, K Carville, S Fletcher, K Honeyman, S Agrawal, ...
Neuromuscular disorders 9 (5), 330-338, 1999
Detection and identification of multiple mycobacterial pathogens by DNA amplification in a single tube.
S Wilton, D Cousins
Genome Research 1 (4), 269-273, 1992
Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD
G McClorey, HM Moulton, PL Iversen, S Fletcher, SD Wilton
Gene therapy 13 (19), 1373-1381, 2006
Mutations in the nebulin gene associated with autosomal recessive nemaline myopathy
K Pelin, P Hilpelä, K Donner, C Sewry, PA Akkari, SD Wilton, ...
Proceedings of the National Academy of Sciences 96 (5), 2305-2310, 1999
A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse
PN Porensky, C Mitrpant, VL McGovern, AK Bevan, KD Foust, BK Kaspar, ...
Human molecular genetics 21 (7), 1625-1638, 2012
Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle
BL Gebski, CJ Mann, S Fletcher, SD Wilton
Human molecular genetics 12 (15), 1801-1811, 2003
Use of polymerase chain reaction for rapid diagnosis of tuberculosis
DV Cousins, SD Wilton, BR Francis, BL Gow
Journal of Clinical Microbiology 30 (1), 255-258, 1992
Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy
CJ Mann, K Honeyman, G McClorey, S Fletcher, SD Wilton
The Journal of Gene Medicine: A cross‐disciplinary journal for research on …, 2002
Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide
S Fletcher, K Honeyman, AM Fall, PL Harding, RD Johnsen, SD Wilton
The Journal of Gene Medicine: A cross‐disciplinary journal for research on …, 2006
Current status of pharmaceutical and genetic therapeutic approaches to treat DMD
C Pichavant, A Aartsma-Rus, PR Clemens, KE Davies, G Dickson, ...
Molecular Therapy 19 (5), 830-840, 2011
Comparative analysis of antisense oligonucleotide sequences for targeted skipping of exon 51 during dystrophin pre-mRNA splicing in human muscle
V Arechavala-Gomeza, IR Graham, LJ Popplewell, AM Adams, ...
Human gene therapy 18 (9), 798-810, 2007
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